The Trial has begun!! There are announcements from London!! The first patients have been administered the ISIS HTT ! Hugh prayers for us all!!

The first few patients have received doses of an experimental RNA-targeting drug for Huntington's disease, it was announced today.

The trial aims to test the safety of an experimental drug known as ISIS-HTTRx, discovered and developed by Isis Pharmaceuticals. Administered by injection into spinal fluid to improve its delivery to the brain, the drug is the first tested in patients that targets the known cause of the disease: a toxic protein called mutant huntingtin which slowly damages and kills neurons, leading to the progressive and ultimately fatal decline in mental and physical abilities that is the devastating hallmark of Huntington's disease.

[medicalxpress.com]

It is soo tough not to be excited!!!

I am!!!

Will

Did you see that ISIS, or IONIS (they changed they're name for obvious reasons) got FDA orphan status!!! That should bring the trials our way I would hope!! HOPE!!!

I think it is awesome too. I hope it works.